Cell and gene therapies are currently niche products, even within specialty pharmacy, drugs that, by most definitions, are ...
Learn about the groundbreaking gene therapy for sickle cell disease at Manning Family Children's Hospital in Louisiana, ...
Globally, and particularly in the U.S., new frameworks are creating genuine opportunities for earlier collaboration.
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$3 million prize goes to duo whose research led to first sickle cell CRISPR therapy
Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a functional cure for the deadly blood disorders sickle cell disease and beta ...
Three 2026 Breakthrough Prize winners reflect on developing Luxturna, a gene therapy that treats blindness caused by rare ...
Two papers published in The New England Journal of Medicine highlight the potential of gene editing for treatment of sickle ...
Increasingly complex cell therapy modalities, including multi-edit knock-in/knockout designs, are accelerating adoption of ...
Cell and gene therapies have a huge curative potential but come with a large price tag that can result in access barriers. At ...
After six weeks in the hospital, 23‑year‑old Daniel Cressy leaves with hope for a functional cure and a future where he can ...
EQUIGENE Therapeutics, a new spin-off biotech anchored by world-class hematology experts, marks a pivotal step in the UAE’s ...
Comprehending the spate of recent rejections in the cell and gene therapy space may require looking no further than ...
Scientists at the University College London (UCL) have developed a novel therapy that helps treat patients with T cell acute lymphoblastic leukemia (T-ALL). This form of therapy used genome editing ...
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