Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date ...
A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...
In May, a historic moment in science and medicine was captured in a single photo that circulated across news outlets ...
New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...
29d
Gene editing is being sold on the promise of healthier babies — but what are the ethical concerns?
The race to advance gene editing tech continues, spurred on by starry-eyed Silicon Valley investors, entrepreneurs and even ...
Researchers have achieved the first demonstration in mice of using gene therapy to reverse hallmark symptoms of ...
The U.S. Food and Drug Administration (FDA) on Monday extended its review timeline for REGENXBIO Inc.’s (NASDAQ:RGNX) Biologics License Application (BLA) for clemidsogene lanparvovec (RGX-121) for ...
A new gene therapy approach aimed at protecting people with type 1 diabetes from developing diabetic kidney disease—a serious ...
Researchers have understood for decades that some forms of deafness are inherited, yet until now, few of those genetic clues ...
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