Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date ...

New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...

A one-time gene therapy using a patient’s own stem cells has effectively cured a deadly immune disorder in 95% of treated ...

F or children born with severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID), an investigational ...

In a study published in Nature Medicine, Leone and her team reported the first targeted gene therapy to restore myelin, the ...

Treatment introduces an expansion of the scope of gene therapies that might lead to similar treatments for neurodegenerative diseases in other parts of the body ...

After axing a wide swath of federal research projects and grants, a recent slew of awards offers a glimpse into the kinds of ...

Fractyl Health Inc. (NASDAQ:GUTS) is one of the best young stocks with huge upside potential. On October 7, Fractyl Health ...

Immusoft of CA, a clinical stage, engineered B cell company, today announced a historic achievement: the safe and well-tolerated re-dosing of a patient with a gene modified therapeutic product ...

Scientists have found a new way to stop cancer growth without damaging healthy cells. Researchers from the Francis Crick Institute and Vividion Therapeutics discovered a compound that blocks the ...

As industry leaders gather at the annual event in Phoenix, the cell and gene therapy space remains in a state of flux, with M ...