Dr. Marty Makary noted it had "record speed approval," the fastest approval of any gene therapy device combination in U.S.

Three 2026 Breakthrough Prize winners reflect on developing Luxturna, a gene therapy that treats blindness caused by rare ...

The therapy is part of a plan to develop gene therapies that can be efficiently delivered at lower doses, enabling them to be used against more than just “ultra-rare” conditions.

A first-of-its-kind gene therapy that can restore hearing in children born deaf has just cleared its final hurdle—and, in a ...

Danish dermatology specialist Leo Pharma is paying $50 million for U.S. gene writing biotech Replay and its preclinical gene ...

After some tough feedback from the FDA on the path forward for its lead gene therapy, Passage Bio has launched a strategic ...

Saffie Sandford was born with Leber's Congenital Amaurosis and "missed out on a lot" due to difficulties seeing in any ...

Regeneron’s drug restored hearing in 11 of 12 children in a rare, inherited condition that causes deafness.

Sean Davies has a rare inherited form of MND and says he has benefited from specialist treatment.

EQUIGENE Therapeutics, a new spin-off biotech anchored by world-class hematology experts, marks a pivotal step in the UAE’s ...

Regeneron will make its newly approved gene therapy available for free in the U.S. The company hasn't yet decided how much it ...

Regeneron is seeing double-digit revenue growth and has more than 50 therapies in its pipeline, making it a good long-term ...