At just 26 months old, Grace Visser was diagnosed with Rett Syndrome, a rare genetic disorder that affects brain development.

Along with trofinetide to treat Rett Syndrome, Neuren has developed its second drug ... Neurizon said there was no cure for the ultimately fatal ALS/MND, marked by the gradual breakdown of nerve cells ...

The first of which is that the company is gearing up to release additional results from its phase 1/2 study using NGN-401 for the treatment of women with Rett Syndrome. Such additional data is ...

Ahead of his interview at Curepedia: An A-Z of The Cure at the Sugar Club, Dublin on 11 April, the band's biographer Simon Price rounds up his choice of the finest Cure B-sides "The first thing I ...

You can then select "Fine. I'll help you." Grakohr will be pleased, and will breathlessly explain he needs a cure from a book nearby. Be sure not to interrupt him speaking! If you were thorough ...

Researchers at the Josep Carreras Leukaemia Research Institute revealed a new aspect of Rett Syndrome’s pathogenesis that can lead to new therapeutical approaches in the future. According to the ...

It’s hard for patients to comprehend how they could lose an undiscovered cure. Yet “all the people out there who have, you know, sick parents, sick children, this is going to impact,” said ...